Researchclopedia

Research Researchers Institutions Topics Submit About

Command Palette

Search for a command to run...

Researchclopedia

Research Researchers Institutions About

© 2026 Researchclopedia. Powered by OpenAlex under CC0 license.

Regenxbio (United States) | Researchclopedia

Back to institutions

Regenxbio (United States)

Rockvillecompany

145

Works

6,478

Citations

36

h-index

Top Research Topics

Virus-based gene therapy research Lysosomal Storage Disorders Research CRISPR and Genetic Engineering

Top Researchers

Andrew Y. Ng University of Bonn

389 works129,364 citationsh-index: 125

Recent Research

Defining Bayley Scales of Infant and Toddler Development Third Edition (BSITD-III) meaningful change and item relevance in children with neuronopathic MPS II: a caregiver interview-based study

Dawn Phillips,Catherine Wilson,et al.

20260 citations

CAR-T cell therapy research

Retinal Development and Disorders

Viral Infectious Diseases and Gene Expression in Insects

Trypanosoma species research and implications

Monoclonal and Polyclonal Antibodies Research

Biosimilars and Bioanalytical Methods

Muscle Physiology and Disorders

RNA Interference and Gene Delivery

Retinal Diseases and Treatments

C. Tully Princeton University

2,641 works118,220 citationsh-index: 143

Lin Yang Hebei Medical University

467 works38,108 citationsh-index: 61

Ting Chen Fujian Medical University

346 works19,413 citationsh-index: 47

267 works16,133 citationsh-index: 66

Jianguo Gu Nanjing University of Science and Technology

220 works13,125 citationsh-index: 60

Assessment of Immune Responses Against AAV Encoded Transgene Products

Boris Gorovits,Mitra Azadeh,et al.

20262 citations

Study Designs and Crafting Endpoints for Gene Therapy Development Programs in Rare Disease: A Narrative Review

Lindsey Murray,Yin Yin,et al.

20250 citations

2025 White Paper on Recent Issues in Bioanalysis: Redosing Patients with AAV Gene Therapy; CRS Immunogenicity Risk; Shedding Assays; NHP Studies Immunogenicity; CMC vs Bioanalytical Assays; Artificial Intelligence-Powered Genomic Pipelines for NGS ( <u>PART 3A</u> – Recommendations on Gene, Cell, and Vaccine Therapies Immunogenicity & Technologies; Biotherapeutics & Biosimilars Immunogenicity Assessment & Clinical Relevance <u>PART 3B</u> – Regulatory Agencies’ Input on Immunogenicity/Technologies of Biotherapeutics, Gene, Cell & Vaccine Therapies)

Omar Tounekti,Sophie Shubow,et al.

20250 citations

Covary: A translation-aware framework for alignment-free phylogenetics using machine learning

Marvin De los Santos

20250 citations

Re-evaluating acceptable risk of death from gene therapy: A threshold study among individuals with Duchenne muscular dystrophy and their caregivers in the US and UK

Holly L. Peay,Ryan Fischer,et al.

20250 citations