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BioMarin (United Kingdom) | Researchclopedia
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BioMarin (United Kingdom)
London
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Metabolism and Genetic Disorders
Glycogen Storage Diseases and Myoclonus
Health Systems, Economic Evaluations, Quality of Life
Lipid metabolism and disorders
Blood Coagulation and Thrombosis Mechanisms
Neonatal Health and Biochemistry
Diet and metabolism studies
Folate and B Vitamins Research
Myasthenia Gravis and Thymoma
Barbara K. Burton
Lurie Children's Hospital
417 works
13,108 citations
h-index: 64
Effect of vosoritide on genu varum in children with achondroplasia after 1 year in randomized placebo-controlled trials
Klane K. White
,
Melita Irving
,
et al.
2026
0 citations