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Telethon Foundation | Researchclopedia

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Telethon Foundation

Romenonprofit

184

Works

26,171

Citations

77

h-index

Top Research Topics

Virus-based gene therapy research Genomics and Rare Diseases CRISPR and Genetic Engineering

Top Researchers

Andrea Ballabio

583 works75,013 citationsh-index: 120

Recent Research

Etuvetidigene autotemcel for the treatment of Wiskott-Aldrich Syndrome

Francesca Ferrua,Sabina Cenciarelli,et al.

20251 citations

Neurogenetic and Muscular Disorders Research

Neuroscience and Neuropharmacology Research

CAR-T cell therapy research

Muscle Physiology and Disorders

Retinal Development and Disorders

RNA Interference and Gene Delivery

Lysosomal Storage Disorders Research

Immune Cell Function and Interaction

T-cell and B-cell Immunology

Cristina Basso University of Padua

1,121 works70,244 citationsh-index: 124

Stefano Volinia University of Ferrara

505 works57,457 citationsh-index: 91

Marco Sandri University of Padua

283 works49,954 citationsh-index: 89

Elia Stupka Istituti di Ricovero e Cura a Carattere Scientifico

104 works40,890 citationsh-index: 42

Flora Peyvandi University of Milan

1,045 works35,873 citationsh-index: 83

Lentiviral hematopoietic stem and progenitor cell gene therapy for Wiskott-Aldrich Syndrome: Early access experience in Italian patients based on 648/1996 law

Sabina Cenciarelli,Stefania Giannelli,et al.

20250 citations

Lentiviral hematopoietic stem and progenitor cell gene therapy with Etuvetidigene autotemcel for the treatment of Wiskott-Aldrich Syndrome

Francesca Ferrua,Sabina Cenciarelli,et al.

20250 citations

543PGlobal insights into limb girdle muscular dystrophies from the TREAT-NMD global registries network

S. F. McDonald,A. Poll,et al.

20250 citations

197PThe landscape of FSHD data collection: a 2025 expansion to the TREAT-NMD FSHD dataset

M. Garrow,A. Poll,et al.

20250 citations

A roadmap for personalized medicine: the findings of the IC2PerMed project

Flavia Beccia,Francesco Andrea Causio,et al.

20250 citations