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Phase 2a Study of Ataluren-Mediated Dystrophin Production in Patients with Nonsense Mutation Duchenne Muscular Dystrophy
2013
241 citations
Journal Article
gold Open Access
Field-Weighted Citation Impact:
11.32
Phase 2a Study of Ataluren-Mediated Dystrophin Production in Patients with Nonsense Mutation Duchenne Muscular Dystrophy | Researchclopedia
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PTC Therapeutics (United States)
Valerie Northcutt
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PTC Therapeutics (United States)
Gary Elfring
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PTC Therapeutics (United States)
Jay Barth
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PTC Therapeutics (United States)
Stuart W. Peltz
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PTC Therapeutics (United States)