GENERATING HEALTH TECHNOLOGY ASSESSMENT EVIDENCE FOR RARE DISEASES

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Authors

Karen Facey · Evidence Based Research (United States)

Alı́cia Granados

Gordon Guyatt · McMaster University

Alastair Kent · Genetic Alliance UK (United Kingdom)

Nilay D. Shah · Mayo Clinic

Gert Jan van der Wilt · Radboud University Medical Center

Durhane Wong‐Rieger · National Organization for Rare Disorders

Abstract

International consensus is needed on ways to improve evidence collection and assessment of technologies for rare diseases, which recognize the value of novel study designs and analyses in a setting where the outcomes and effects of importance are yet to be agreed.

Topics & Keywords

Health Systems, Economic Evaluations, Quality of Life Pharmaceutical studies and practices Genomics and Rare Diseases

Publication Details

Published in: International Journal of Technology Assessment in Health Care

Volume 30, Issue 4, pp. 416-422

DOI: 10.1017/s0266462314000464

Field-Weighted Citation Impact: 19.29

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GENERATING HEALTH TECHNOLOGY ASSESSMENT EVIDENCE FOR RARE DISEASES

Authors

Abstract

Topics & Keywords

Publication Details