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Miglustat in adult and juvenile patients with Niemann–Pick disease type C: Long-term data from a clinical trial
2009
208 citations
Journal Article
Field-Weighted Citation Impact:
8.77
·
Actelion (Switzerland)
Marc C. Patterson
·
Mayo Clinic in Arizona
Miglustat in adult and juvenile patients with Niemann–Pick disease type C: Long-term data from a clinical trial | Researchclopedia