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A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice
2016
553 citations
Journal Article
green Open Access
Field-Weighted Citation Impact:
41.68
A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice | Researchclopedia
University of Pennsylvania
Chenyu Xu
·
Children's National
Hiroki Morizono
·
Children's National
Kiran Musunuru
·
Harvard University
Mark L. Batshaw
·
Children's National
James M. Wilson
·
University of Pennsylvania