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The validation of pharmacogenetics for the identification of Fabry patients to be treated with migalastat
2016
207 citations
Journal Article
bronze Open Access
Field-Weighted Citation Impact:
10.12
The validation of pharmacogenetics for the identification of Fabry patients to be treated with migalastat | Researchclopedia
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Boston Biomedical (United States)
Hadis Williams
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Amicus Therapeutics (United States)
Julie Yu
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Amicus Therapeutics (United States)
Daniel G. Bichet
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Hôpital du Sacré-Cœur de Montréal
Dominique P. Germain
Roberto Giugliani
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National Institute on Population Medical Genetics
Derralynn Hughes
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University College London
Raphael Schiffmann
William R. Wilcox
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Emory University
Robert J. Desnick
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Icahn School of Medicine at Mount Sinai
John Kirk
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Amicus Therapeutics (United States)
Jay Barth
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Amicus Therapeutics (United States)
Carrolee Barlow
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Amicus Therapeutics (United States)
Kenneth J. Valenzano
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Amicus Therapeutics (United States)
Jeff Castelli
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Amicus Therapeutics (United States)
David J. Lockhart
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Amicus Therapeutics (United States)