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Patient Voice in Rare Disease Drug Development and Endpoints

201622 citationsJournal Article

Authors

Linda S. Deal · Pfizer (United States)

Jonathan C. Goldsmith · Center for Drug Evaluation and Research

Susan Martin · RTI Health Solutions

Ann Barbier · Agios Pharmaceuticals (United States)

Steven L. Roberds

David H. Schubert · Stealth BioTherapeutics (United States)

Topics & Keywords

Autism Spectrum Disorder Research Genomics and Rare Diseases Pharmaceutical studies and practices

UN Sustainable Development Goals

Good health and well-being

Publication Details

Published in: Therapeutic Innovation & Regulatory Science

Volume 51, Issue 2, pp. 257-263

DOI: 10.1177/2168479016671559

Field-Weighted Citation Impact: 0.17

Patient Voice in Rare Disease Drug Development and Endpoints | Researchclopedia