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VTS-270 for the treatment of Niemann-Pick disease type C | Researchclopedia

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VTS-270 for the treatment of Niemann-Pick disease type C

20173 citationsJournal Article

Authors

Bernardus N Machielse · Vtesse (United States)

Forbes D. Porter · Eunice Kennedy Shriver National Institute of Child Health and Human Development

Alfred L. Yergey · National Institutes of Health

Elizabeth Berry‐Kravis · Rush University Medical Center

Allan Darling · Vtesse (United States)

Ravi Rao · Vtesse (United States)

Topics & Keywords

Lysosomal Storage Disorders Research Child Nutrition and Feeding Issues Adolescent and Pediatric Healthcare

Publication Details

Published in: Molecular Genetics and Metabolism

Volume 120, Issue 1-2, pp. S89-S90

DOI: 10.1016/j.ymgme.2016.11.219

Field-Weighted Citation Impact: 0.00