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Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy | Researchclopedia
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Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy
2018
1,402 citations
Journal Article
green Open Access
Field-Weighted Citation Impact:
97.68
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The University of Texas Southwestern Medical Center
Janbernd Kirschner
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University Medical Center Freiburg
Nancy L. Kuntz
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Lurie Children's Hospital
Kayoko Saito
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Tokyo Women's Medical University
Perry B. Shieh
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University of California, Los Angeles
M. Tulinius
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Drottning Silvias barn- och ungdomssjukhus
Elena Mazzone
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Catholic University of America
Jacqueline Montes
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Columbia University Irving Medical Center
Kathie M. Bishop
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Ionis Pharmaceuticals (United States)
Qingqing Yang
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Ionis Pharmaceuticals (United States)
Richard Foster
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Biogen (United States)
Sarah Gheuens
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Biogen (United States)
C. Frank Bennett
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Ionis Pharmaceuticals (United States)
Wildon Farwell
·
Biogen (United States)
Eugene Schneider
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Ionis Pharmaceuticals (United States)
Darryl C. De Vivo
Richard S. Finkel
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Nemours Children's Clinic