An overview of the Cure SMA membership database: Highlights of key demographic and clinical characteristics of SMA members

201849 citationsJournal Articlegreen Open Access

Authors

Lisa Belter · Cure Spinal Muscular Atrophy

Suzanne F. Cook

Thomas O. Crawford · Johns Hopkins Hospital

Jill Jarecki · Cure Spinal Muscular Atrophy

Cynthia C. Jones · Biogen (United States)

John T. Kissel · The Ohio State University

Mary Schroth · Cure Spinal Muscular Atrophy

Abstract

The Cure SMA database is a unique and robust source of patient reported data that informs on the burden of illness and supports the development of new therapeutic modalities.

Topics & Keywords

Neurogenetic and Muscular Disorders Research Cardiac Structural Anomalies and Repair MXene and MAX Phase Materials

UN Sustainable Development Goals

Good health and well-being

Publication Details

Published in: Journal of Neuromuscular Diseases

Volume 5, Issue 2, pp. 167-176

DOI: 10.3233/jnd-170292

Field-Weighted Citation Impact: 3.49