Cardiac and skeletal muscle effects in the randomized HOPE-Duchenne trial

201982 citationsJournal Articlebronze Open Access

Authors

Michael D. Taylor · Cedars-Sinai Medical Center

John L. Jefferies · Cedars-Sinai Medical Center

Barry J. Byrne · Cedars-Sinai Medical Center

João A.C. Lima · Cedars-Sinai Medical Center

Bharath Ambale‐Venkatesh · Cedars-Sinai Medical Center

Mohammad R. Ostovaneh · Cedars-Sinai Medical Center

Raj Makkar

Abstract

This phase I/II study provides Class II evidence that for patients with DMD, intracoronary CAP-1002 is feasible and appears safe and potentially effective.

Topics & Keywords

Muscle Physiology and Disorders Tissue Engineering and Regenerative Medicine Prosthetics and Rehabilitation Robotics

UN Sustainable Development Goals

Good health and well-being

Publication Details

Published in: Neurology

Volume 92, Issue 8, pp. e866-e878

DOI: 10.1212/wnl.0000000000006950

Field-Weighted Citation Impact: 4.71