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Lentiviral gene therapy for X-linked chronic granulomatous disease

2020246 citationsJournal Articlegreen Open Access

Authors

Donald B. Kohn · University of California, Los Angeles

Claire Booth · Great Ormond Street Hospital for Children NHS Foundation Trust

Elizabeth M. Kang · National Institutes of Health

Sung‐Yun Pai · Boston Children's Hospital

Kit L. Shaw · University of California, Los Angeles

Giorgia Santilli · Great Ormond Street Hospital for Children NHS Foundation Trust

Topics & Keywords

Virus-based gene therapy research Neutrophil, Myeloperoxidase and Oxidative Mechanisms CRISPR and Genetic Engineering

UN Sustainable Development Goals

Good health and well-being

Publication Details

Published in: Nature Medicine

Volume 26, Issue 2, pp. 200-206

DOI: 10.1038/s41591-019-0735-5

Field-Weighted Citation Impact: 30.96

Lentiviral gene therapy for X-linked chronic granulomatous disease | Researchclopedia

· Boston Children's Hospital

Karen Buckland · Great Ormond Street Hospital for Children NHS Foundation Trust

Uimook Choi · National Institutes of Health

Suk See De Ravin · National Institutes of Health

Morna J. Dorsey · University of California, San Francisco

Caroline Y. Kuo · University of California, Los Angeles

Diego León‐Rico · Great Ormond Street Hospital for Children NHS Foundation Trust

Christine Rivat · Great Ormond Street Hospital for Children NHS Foundation Trust

Natalia Izotova · Great Ormond Street Hospital for Children NHS Foundation Trust

Kimberly Gilmour · Great Ormond Street Hospital for Children NHS Foundation Trust

Katie Snell · Great Ormond Street Hospital for Children NHS Foundation Trust

Jinhua Xu-Bayford Dip · Great Ormond Street Hospital for Children NHS Foundation Trust

Jinan Darwish · Great Ormond Street Hospital for Children NHS Foundation Trust

Emma Morris · University College London Hospitals NHS Foundation Trust

Dayna Terrazas · University of California, Los Angeles

Leo D. Wang · Boston Children's Hospital

Christopher Bauser · Eurofins (Germany)

Tobias Paprotka · Eurofins (Germany)

Douglas B. Kuhns · Leidos (United States)

John Gregg · University of Pennsylvania

Hayley E. Raymond · University of Pennsylvania

J.K. Everett · University of Pennsylvania

Géraldine Honnet · Genethon (France)

Luca Biasco · Great Ormond Street Hospital for Children NHS Foundation Trust

Peter E. Newburger · University of Massachusetts Chan Medical School

Frederic D. Bushman · University of Pennsylvania

Manuel Grez · Georg Speyer Haus

H. Bobby Gaspar · Great Ormond Street Hospital for Children NHS Foundation Trust

David A. Williams · Boston Children's Hospital

Harry L. Malech · National Institutes of Health

Anne Galy · Inserm

Adrian J. Thrasher · Great Ormond Street Hospital for Children NHS Foundation Trust