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Long-Term Follow-Up of the First in Human Intravascular Delivery of AAV for Gene Transfer: AAV2-hFIX16 for Severe Hemophilia B
2020
200 citations
Journal Article
green Open Access
Field-Weighted Citation Impact:
21.82
Long-Term Follow-Up of the First in Human Intravascular Delivery of AAV for Gene Transfer: AAV2-hFIX16 for Severe Hemophilia B | Researchclopedia
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University of Pennsylvania
Alexa R. Runowski
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Children's Hospital of Philadelphia
Jennifer Wellman
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Spark Therapeutics (United States)
Katie Wachtel
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Spark Therapeutics (United States)
Yifeng Chen
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Spark Therapeutics (United States)
Xavier M. Anguela
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Spark Therapeutics (United States)
Klaudia Kuranda
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Spark Therapeutics (United States)
Federico Mingozzi
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Spark Therapeutics (United States)
Katherine A. High
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Spark Therapeutics (United States)