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AAV gene therapy for Tay-Sachs disease

2022128 citationsJournal Articlegreen Open Access

Authors

Terence R. Flotte · UMass Memorial Health Care

Oğuz Çataltepe · University of Massachusetts Chan Medical School

Ajit S Puri · University of Massachusetts Chan Medical School

Ana Rita Batista · University of Massachusetts Chan Medical School

Richard P. Moser · University of Massachusetts Chan Medical School

Diane McKenna‐Yasek · University of Massachusetts Chan Medical School

Topics & Keywords

Neurogenetic and Muscular Disorders Research Lysosomal Storage Disorders Research Autism Spectrum Disorder Research

UN Sustainable Development Goals

Good health and well-being

Publication Details

Published in: Nature Medicine

Volume 28, Issue 2, pp. 251-259

DOI: 10.1038/s41591-021-01664-4

Field-Weighted Citation Impact: 17.75

AAV gene therapy for Tay-Sachs disease | Researchclopedia

Catherine Douthwright

· University of Massachusetts Chan Medical School

Gwladys Gernoux · University of Massachusetts Chan Medical School

Meghan Blackwood · University of Massachusetts Chan Medical School

Christian Mueller · University of Massachusetts Chan Medical School

Phillip W.L. Tai · University of Massachusetts Chan Medical School

Xuntian Jiang · Washington University in St. Louis

Scot T. Bateman · University of Massachusetts Chan Medical School

Spiro G. Spanakis · University of Massachusetts Chan Medical School

Julia Parzych · University of Massachusetts Chan Medical School

Allison M. Keeler · University of Massachusetts Chan Medical School

Aly Abayazeed · University of Massachusetts Chan Medical School

Saurabh Rohatgi · University of Massachusetts Chan Medical School

Laura Gibson · University of Massachusetts Chan Medical School

Robert W. Finberg · University of Massachusetts Chan Medical School

Bruce Barton · University of Massachusetts Chan Medical School

Zeynep Vardar · University of Massachusetts Chan Medical School

Mohammed Salman Shazeeb · University of Massachusetts Chan Medical School

Matthew J. Gounis · University of Massachusetts Chan Medical School

Cynthia J. Tifft · National Institutes of Health

Florian Eichler · Harvard University

Robert H. Brown · University of Massachusetts Chan Medical School

Douglas R. Martin · Auburn University

Heather Gray‐Edwards · University of Massachusetts Chan Medical School

Miguel Sena‐Esteves · UMass Memorial Health Care