Effect of Ataluren on Age at Loss of Ambulation in Nonsense Mutation Duchenne Muscular Dystrophy: Observational Data from the STRIDE Registry (P1.6-067)

In this study, age at loss of ambulation was evaluated in patients with nmDMD taking ataluren for at least 12 months while enrolled in the international, multi-center STRIDE (Strategic Targeting of Registries and International Datasets of Excellence) Registry (N=207).