Rycal S48168 (ARM210) for RYR1-related myopathies: a phase one, open-label, dose-escalation trial

202422 citationsJournal Articlegold Open Access

Authors

Joshua J. Todd · National Institute of Nursing Research

Tokunbor A. Lawal · National Institutes of Health

Irene C. Chrismer · National Institute of Nursing Research

Angela Kokkinis · National Institutes of Health

Christopher Grunseich · National Institutes of Health

Minal Jain · National Institutes of Health

M. Waite

Abstract

NINDS and NINR Intramural Research Programs, NIH Clinical Center Bench to Bedside Award (2017-551673), ARMGO Pharma Inc., and its development partner Les Laboratoires Servier.

Topics & Keywords

Ion channel regulation and function Cardiac electrophysiology and arrhythmias Calcium signaling and nucleotide metabolism

UN Sustainable Development Goals

Good health and well-being

Publication Details

Published in: EClinicalMedicine

Volume 68, pp. 102433-102433

DOI: 10.1016/j.eclinm.2024.102433

Field-Weighted Citation Impact: 5.01

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