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Design considerations for <i>C9orf72</i> disease prevention trials
2025
2 citations
Journal Article
hybrid Open Access
Field-Weighted Citation Impact:
2.81
Design considerations for <i>C9orf72</i> disease prevention trials | Researchclopedia
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Jacksonville University
Edward D. Huey
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Brown University
Martin R. Turner
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University of Oxford
Eric A. Macklin
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Massachusetts General Hospital
James D. Berry
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Massachusetts General Hospital
Corey T. McMillan
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University of Pennsylvania
Tania Gendron
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Mayo Clinic in Florida
Chiadi U. Onyike
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Johns Hopkins University
Howard J. Rosen
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University of California, San Francisco
Hilary W. Heuer
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University of California, San Francisco
Anne‐Laure Grignon
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University of Miami
Kuldip D. Dave
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Amyotrophic Lateral Sclerosis Association
Calaneet Balas
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Amyotrophic Lateral Sclerosis Association
Amanda M. Gleixner
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Dementia UK
Andrew Satlin
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Seelos Therapeutics (United States)
Billy Dunn
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Michael J. Fox Foundation
Penny A. Dacks
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Dementia UK
Adam L. Boxer
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University of California, San Francisco