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Effectiveness of Ataluren in Patients with nmDMD: Confirmatory Evidence from the STRIDE Registry
2025
0 citations
Journal Article
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Effectiveness of Ataluren in Patients with nmDMD: Confirmatory Evidence from the STRIDE Registry | Researchclopedia
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Universidade de São Paulo
Craig M. McDonald
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University of California, Davis
Heather Gordish‐Dressman
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Children's National
L. Morgenroth
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BioHybrid Solutions (United States)
Shelley Johnson
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PTC Therapeutics (United States)
Alexis Krolick
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PTC Therapeutics (United States)
B. Anbu
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PTC Therapeutics (United States)
Enwu Liu
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PTC Therapeutics (United States)
Francesco Muntoni
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Great Ormond Street Hospital