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Regulatory sandboxes: A new frontier for rare disease therapies

20250 citationsJournal Articlediamond Open Access

Authors

Galliano Zanello · Care-for-Rare Foundation

Violeta Stoyanova‐Beninska · European Medicines Agency

Oxana Iliach · Certara (United States)

Daniel Scherman · Centre National de la Recherche Scientifique

Samantha Parker · Clinical Research Consortium

David A. Pearce · University of South Dakota

Topics & Keywords

Genomics and Rare Diseases Autism Spectrum Disorder Research Pharmaceutical studies and practices

Publication Details

Published in: Rare

Volume 3, pp. 100110-100110

DOI: 10.1016/j.rare.2025.100110

Field-Weighted Citation Impact: 0.00

Regulatory sandboxes: A new frontier for rare disease therapies | Researchclopedia