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Potential One-Time Lipid Nanoparticle-Driven Gene Editing Therapy to Address ADPKD Caused by PKD1 Mutations
2025
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Journal Article
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Potential One-Time Lipid Nanoparticle-Driven Gene Editing Therapy to Address ADPKD Caused by PKD1 Mutations | Researchclopedia
Rohini Kalvakuntla
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Helicos Biosciences (United States)
Anirudh Nishtala
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Helicos Biosciences (United States)