A novel modifier gene therapy to treat Stargardt disease: Phase 1 GARDian1 Trial Insights

20261 citationsJournal Articlehybrid Open Access

Authors

Abstract

1 Change in Atrophic Lesion Growth and Visual Acuity at M12 following OCU410ST Treatment.Treated eyes showed a decrease in atrophic lesion growth from baseline (a), and stabilisation/improvement in Visual Acuity (b).

Topics & Keywords

Retinal Development and Disorders Connexins and lens biology Virus-based gene therapy research

UN Sustainable Development Goals

Zero hunger

Publication Details

Published in: Eye

Volume 40, Issue 3, pp. 429-430

DOI: 10.1038/s41433-025-04202-5

Field-Weighted Citation Impact: 25.87