Baseline analysis of patient reported outcomes in the progressive familial intrahepatic cholestasis patient registry

20260 citationsJournal Article

Authors

R. Daryl Fischer · Children's Mercy Hospital

Emily Ventura · Kentucky Educational Television

James E. Squires · Children's Hospital of Pittsburgh

Wálter Pérez · Kentucky Educational Television

Akihiro Asai · Cincinnati Children's Hospital Medical Center

Melissa Kochanowsky · Kentucky Educational Television

Benjamin L. Shneider

Abstract

The PNPR fills a previously identified gap in PFIC research-the lack of PROs-and reveals the negative impact of disease and pruritus on patient and family function, QoL indicators, finances, and measures of general health.

Topics & Keywords

Drug Transport and Resistance Mechanisms Pediatric Hepatobiliary Diseases and Treatments Liver Diseases and Immunity

Publication Details

Published in: Journal of Pediatric Gastroenterology and Nutrition

DOI: 10.1002/jpn3.70366

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Baseline analysis of patient reported outcomes in the progressive familial intrahepatic cholestasis patient registry

Authors

Abstract

Topics & Keywords

Publication Details