Ketogenic drug tricaprilin (CER-0001) for the treatment of refractory infantile epileptic spasms: a phase 1/2a study

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Authors

Marc Cantillon · Johnson University

Sylvia Chen · SMEC (Australia)

Nikki McIntyre · SMEC (Australia)

Samuel T. Henderson · SMEC (Australia)

Kate Riney · The University of Queensland

Dick C. Chan · KK Women's and Children's Hospital

John Lawson ·

Abstract

Our findings demonstrate that CER-0001 offers a novel potential treatment option as a prescription drug for ketogenic therapy, without the restrictions imposed by KDs.

Topics & Keywords

Diet and metabolism studies Epilepsy research and treatment Gastroesophageal reflux and treatments

UN Sustainable Development Goals

Good health and well-being

Publication Details

Published in: Frontiers in Pediatrics

Volume 13, pp. 1575014-1575014

DOI: 10.3389/fped.2025.1575014

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