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CRISPR-Cas12a Gene Editing of <i>HBG1</i> and <i>HBG2</i> Promoters to Treat Sickle Cell Disease
2026
3 citations
Journal Article
Field-Weighted Citation Impact:
98.24
CRISPR-Cas12a Gene Editing of <i>HBG1</i> and <i>HBG2</i> Promoters to Treat Sickle Cell Disease | Researchclopedia
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Nationwide Children's Hospital
H. J. B. Atkins
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Ottawa Hospital
Akshay Sharma
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St. Jude Children's Research Hospital
Kai-Hsin Chang
Michael Jaskolka
Keunpyo Kim
Qifeng Yu
Baisong Mei
Olubunmi Afonja
Mark C. Walters
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University of California, San Francisco