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Gene Therapy for Leber's Congenital Amaurosis is Safe and Effective Through 1.5 Years After Vector Administration
2009
551 citations
Journal Article
bronze Open Access
Field-Weighted Citation Impact:
21.23
Gene Therapy for Leber's Congenital Amaurosis is Safe and Effective Through 1.5 Years After Vector Administration | Researchclopedia
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University of Campania "Luigi Vanvitelli"
Kathleen Marshall
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Children's Hospital of Philadelphia
Sandro Banfi
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Telethon Institute Of Genetics And Medicine
Enrico Maria Surace
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Telethon Institute Of Genetics And Medicine
Junwei Sun
·
Children's Hospital of Philadelphia
T. Michael Redmond
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National Eye Institute
Xiaosong Zhu
·
Children's Hospital of Philadelphia
Kenneth S. Shindler
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Penn Presbyterian Medical Center
Gui‐Shuang Ying
·
University of Pennsylvania
Carmela Ziviello
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Telethon Institute Of Genetics And Medicine
Carmela Acerra
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University of Naples Federico II
J. Fraser Wright
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University of Pennsylvania
Jennifer Wellman McDonnell
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Children's Hospital of Philadelphia
Katherine A. High
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Howard Hughes Medical Institute
Jean Bennett
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University of Pennsylvania
Alberto Auricchio
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Telethon Institute Of Genetics And Medicine