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Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial
2009
852 citations
Journal Article
Field-Weighted Citation Impact:
30.37
Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial | Researchclopedia
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Children's Hospital of Philadelphia
Jeannette Bennicelli
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University of Pennsylvania
Gui‐Shuang Ying
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University of Pennsylvania
Settimio Rossi
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University of Naples Federico II
Ann Fulton
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Boston Children's Hospital
Kathleen Marshall
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Children's Hospital of Philadelphia
Sandro Banfi
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Telethon Institute Of Genetics And Medicine
Daniel C. Chung
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University of Pennsylvania
Jessica I. W. Morgan
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University of Pennsylvania
Bernd Hauck
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Children's Hospital of Philadelphia
Olga Zelenaia
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Children's Hospital of Philadelphia
Xiaosong Zhu
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Children's Hospital of Philadelphia
Leslie Raffini
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Philadelphia University
Frauke Coppieters
Elfride De Baere
Kenneth S. Shindler
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Penn Presbyterian Medical Center
Nicholas J. Volpe
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University of Pennsylvania
Enrico Maria Surace
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Telethon Institute Of Genetics And Medicine
Carmela Acerra
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University of Naples Federico II
Arkady Lyubarsky
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University of Pennsylvania
T. Michael Redmond
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National Institutes of Health
Edwin M. Stone
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University of Iowa
Junwei Sun
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Children's Hospital of Philadelphia
Jennifer Wellman McDonnell
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Children's Hospital of Philadelphia
Bart P. Leroy
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Ghent University Hospital
Francesca Simonelli
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University of Naples Federico II
Jean Bennett
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Children's Hospital of Philadelphia